Rare Disease Drug Development: What Patients and Advocates Need to Know
Understand the Drug Development Process and the Role Patients and Advocates Can Play
Developing a new treatment is a long, complex, and expensive process. Understanding how it works can help patients, caregivers, and advocates become more informed and engaged partners in rare disease research.
NORD’s Rare Disease Drug Development Series breaks the process down into clear, approachable courses designed with the rare disease community in mind. Explore key stages of drug development, from early research and clinical trials to FDA review and access, and learn how patient and community perspectives can contribute along the way.
The series is free, mobile-friendly, and self-paced. Choose a course above to get started.
Help Others Learn About Rare Disease Drug Development!
Know patients, caregivers, or advocates who could benefit from this series? Use our ready-to-share and customizable promotional materials to spread the word in your community.
